2
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| COG7-congenital disorder of glycosylation | envafolimab | Orphan Designation | - |
| Kabuki syndrome 1 | envafolimab | Orphan Designation | - |
| Smith-Lemli-Opitz syndrome | envafolimab | Orphan Designation | - |
| biliary tract cancer | Envafolimab | Orphan Designation | - |
| gastric cancer | envafolimab | Orphan Designation | - |