3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute graft versus host disease | Teduglutide | Orphan Designation | - |
| inflammatory bowel disease 1 | 5-(4-carboxymethyl-phenylazo)-2-hydroxybenzoic acid disodium salt | Orphan Designation | - |
| pediatric hepatocellular carcinoma | 5-(4-carboxymethyl-phenylazo)-2-hydroxybenzoic acid disodium salt | Orphan Designation | - |
| pediatric-onset Graves disease | 5-(4-carboxymethyl-phenylazo)-2-hydroxybenzoic acid disodium salt | Orphan Designation | - |
| short bowel syndrome | recombinant fusion protein comprising exenatide and XTEN | Orphan Designation | - |