1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| GM1 gangliosidosis | myo-inositol | Orphan Designation | - |
| exudative vitreoretinopathy 1 | myo-inositol | Orphan Designation | - |
| retinopathy of prematurity | myo-inositol | Orphan Designation | - |