1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Spondyloenchondrodysplasia with immune dysregulation | Purified extract of Pseudomonas aeruginosa | Orphan Designation | - |
| acquired purpura fulminans | Purified extract of Pseudomonas aeruginosa | Orphan Designation | - |
| autoimmune thrombocytopenic purpura | Purified extract of Pseudomonas aeruginosa | Orphan Designation | - |