4
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Huntington disease | laquinimod sodium | Orphan Designation | - |
| myelofibrosis | Tasquinimod | Orphan Designation | - |
| plasma cell myeloma | Tasquinimod | Orphan Designation | - |
| systemic sclerosis | paquinimod | Orphan Designation | - |