2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adult neuronal ceroid lipofuscinosis | Zynlonta | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | Zynlonta | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | Zynlonta | Orphan Designation | - |
| adult-onset proximal spinal muscular atrophy, autosomal dominant | Zynlonta | Orphan Designation | - |
| diffuse large B-cell lymphoma | Zynlonta | Orphan Designation | - |
| mantle cell lymphoma | Humanized monoclonal immunoglobulin G1 antibody directed against human CD19 conjugated to SG3199 through a protease cleavable valine-alanine linker | Orphan Designation | - |
| primary adult heart tumor | Zynlonta | Orphan Designation | - |