3
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Koolen-de Vries syndrome due to a point mutation | cethromycin | Orphan Designation | - |
| Prader-Willi syndrome due to translocation | cethromycin | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | cethromycin | Orphan Designation | - |
| congenital anomalies of kidney and urinary tract 3 | cethromycin | Orphan Designation | - |
| neuroacanthocytosis | cethromycin | Orphan Designation | - |
| tularemia | cethromycin | Orphan Designation | - |
| typhoidal tularemia | cethromycin | Orphan Designation | - |
| ulceroglandular tularemia | cethromycin | Orphan Designation | - |