3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | tetra substituted prophyrin derivative containing manganese (III) | Orphan Designation | - |
| amyotrophic lateral sclerosis | [5,10,15,20-tetrakis(1,3-diethylimidazolium-2-yl)porphyrinato] manganese(III)pentachloride | Orphan Designation | - |
| anosmia for isobutyric acid | tetra substituted prophyrin derivative containing manganese (III) | Orphan Designation | - |
| idiopathic pulmonary fibrosis | tetra-substituted porphyrin derivative containing manganese (III) | Orphan Designation | - |
| neuroacanthocytosis | tetra substituted prophyrin derivative containing manganese (III) | Orphan Designation | - |