4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
1
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Guillain-Barre syndrome | nomacopan | Orphan Designation | - |
| bullous pemphigoid | nomacopan | Orphan Designation | - |
| disease related to hematopoietic stem cell transplant | nomacopan | Orphan Designation | - |
| hematopoietic and lymphoid cell neoplasm | nomacopan | Orphan Designation | - |
| hematopoietic and lymphoid system neoplasm | nomacopan | Orphan Designation | - |
| paroxysmal nocturnal hemoglobinuria | nomacopan | Orphan Designation | - |