2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chronic intestinal pseudoobstruction | Velusetrag | Orphan Designation | - |
| polysyndactyly 4 | dihydroartemisinin and piperaquine | Orphan Designation | - |
| pure hereditary spastic paraplegia | dihydroartemisinin and piperaquine | Orphan Designation | - |