1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| EMILIN-1-related connective tissue disease | Kre-Celazine | Orphan Designation | - |
| Spondyloenchondrodysplasia with immune dysregulation | Kre-Celazine | Orphan Designation | - |
| chromosome 15q11.2 deletion syndrome | Kre-Celazine | Orphan Designation | - |
| juvenile idiopathic arthritis | Kre-Celazine | Orphan Designation | - |
| polyarticular juvenile rheumatoid arthritis | Kre-Celazine | Orphan Designation | - |
| systemic-onset juvenile idiopathic arthritis | Kre-Celazine | Orphan Designation | - |