1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 7q11.23 microduplication syndrome | Silver sulfadiazine and cerium nitrate | Orphan Designation | - |
| Kabuki syndrome 1 | Silver sulfadiazine and cerium nitrate | Orphan Designation | - |
| osteopathia striata with cranial sclerosis | Silver sulfadiazine and cerium nitrate | Orphan Designation | - |