1
Orphan Designations
1
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DEGCAGS syndrome | So-Aqueous | Orphan Designation | - |
| idiopathic neonatal atrial flutter | So-Aqueous | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 13 | So-Aqueous | Orphan Designation | - |
| thrombocytopenia-absent radius syndrome | So-Aqueous | Orphan Designation | - |