1
Orphan Designations
1
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| severe Canavan disease | digoxin immune fab (ovine) | Orphan Designation | - |
| severe achondroplasia-developmental delay-acanthosis nigricans syndrome | digoxin immune fab (ovine) | Orphan Designation | - |
| severe pre-eclampsia | digoxin immune fab (ovine) | Orphan Designation | - |