4
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ALK-positive large B-cell lymphoma | Autologous Engineered Skin Substitute | Orphan Designation | - |
| NF2-related schwannomatosis | Autologous Engineered Skin Substitute | Orphan Designation | - |
| fountain syndrome | Autologous Engineered Skin Substitute | Orphan Designation | - |
| glycogen storage disease I | Autologous Engineered Skin Substitute | Orphan Designation | - |
| idiopathic non-lupus full-house nephropathy | Autologous Engineered Skin Substitute | Orphan Designation | - |
| retinal artery occlusion | mesencephalic, astrocyte-derived neurotrophic factor | Orphan Designation | - |
| retinitis pigmentosa | human recombinant mesencephalic, astrocyte derived neurotrophic factor | Orphan Designation | - |