1
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| neurodegeneration with brain iron accumulation 2A | Antithrombin III human | Orphan Designation | - |
| secondary Parkinson disease | Antithrombin III human | Orphan Designation | - |