2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| FOXG1 disorder | tianeptine | Orphan Designation | - |
| Rett syndrome | tianeptine | Orphan Designation | - |
| atypical Rett syndrome | tianeptine | Orphan Designation | - |
| juvenile-onset Steinert myotonic dystrophy | Tideglusib | Orphan Designation | - |
| late-onset Steinert myotonic dystrophy | Tideglusib | Orphan Designation | - |
| myotonic dystrophy type 1 | Tideglusib | Orphan Designation | - |