3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | N-(4-((2-aminopyrimidin-5-yl)ethynyl)-3-fluoropyridin-2-yl)-5-chloro-2-methoxypyridine-3-sulfonamide | Orphan Designation | - |
| adult-onset Still disease | Camoteskimab | Orphan Designation | - |
| dyscalculia | Camoteskimab | Orphan Designation | - |
| pulmonary arterial hypertension | humanized monoclonal antibody directed against human zinc-regulated transporter-like, iron-regulated transporter-like protein 12 | Orphan Designation | - |
| systemic-onset juvenile idiopathic arthritis | Camoteskimab | Orphan Designation | - |