5
Orphan Designations
0
FDA Approvals
16
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| LIPE-related familial partial lipodystrophy | sotalol hydrochloride | Orphan Designation | - |
| central precocious puberty | Triptodur | Orphan Designation | - |
| coccidioidomycosis | Cetylev | Orphan Designation | - |
| gastrointestinal stromal tumor | sotalol hydrochloride | Orphan Designation | - |
| herpes zoster | Horizant | Orphan Designation | - |
| lice infestation | sotalol hydrochloride | Orphan Designation | - |
| necrobiosis lipoidica | Cetylev | Orphan Designation | - |
| neurodegeneration with brain iron accumulation 2A | Cetylev | Orphan Designation | - |
| pediatric acute-onset neuropsychiatric syndrome | Triptodur | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Triptodur | Orphan Designation | - |
| pediatric ovarian dysgerminoma | Triptodur | Orphan Designation | - |
| pediatric ovarian germ cell tumor | Triptodur | Orphan Designation | - |
| pediatric-onset Graves disease | Triptodur | Orphan Designation | - |
| postherpetic neuralgia | Horizant | Orphan Designation | - |
| secondary Parkinson disease | Cetylev | Orphan Designation | - |
| subarachnoid hemorrhage | NYMALIZE | Orphan Designation | - |