1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| autoimmune thrombocytopenic purpura | efgartigimod | Orphan Designation | - |
| inborn error of immunity | efgartigimod | Orphan Designation | - |
| nephrotic syndrome 14 | efgartigimod | Orphan Designation | - |