1
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Crimean-Congo hemorrhagic fever | Mononine | Orphan Designation | - |
| Kaposi's sarcoma | Mononine | Orphan Designation | - |
| Marburg hemorrhagic fever | Mononine | Orphan Designation | - |
| central hypoventilation syndrome, congenital, 1, with or without Hirschsprung disease | Mononine | Orphan Designation | - |
| congenital disorder of glycosylation, type IIz | Mononine | Orphan Designation | - |
| developmental and epileptic encephalopathy, 36 | Mononine | Orphan Designation | - |
| hypermethioninemia with deficiency of S-adenosylhomocysteine hydrolase | Mononine | Orphan Designation | - |
| porencephaly-microcephaly-bilateral congenital cataract syndrome | Mononine | Orphan Designation | - |
| secondary Parkinson disease | Mononine | Orphan Designation | - |