3
Orphan Designations
2
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Finnish type amyloidosis | encorafenib + binimetinib | Orphan Designation | - |
| Hodgkins lymphoma | encorafenib + binimetinib | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | encorafenib + binimetinib | Orphan Designation | - |
| dilated cardiomyopathy | p38 mitogen-activated kinase inhibitor | Orphan Designation | - |
| plasma cell myeloma | filanesib | Orphan Designation | - |
| stage II endometrioid carcinoma | encorafenib + binimetinib | Orphan Designation | - |
| stage IVb bladder cancer | encorafenib + binimetinib | Orphan Designation | - |
| uterine cervix carcinoma in situ | encorafenib + binimetinib | Orphan Designation | - |