3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Finnish type amyloidosis | encorafenib | Orphan Designation | - |
| ovarian cancer | binimetinib | Orphan Designation | - |
| post 5-alpha-reductase inhibitors treatment syndrome | binimetinib | Orphan Designation | - |
| post-treatment Lyme disease syndrome | binimetinib | Orphan Designation | - |
| stage II endometrioid carcinoma | encorafenib | Orphan Designation | - |
| stage IVb bladder cancer | encorafenib | Orphan Designation | - |
| treatment-refractory schizophrenia | binimetinib | Orphan Designation | - |