2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| graft versus host disease | Placenta-Derived Decidua Stromal Cells | Orphan Designation | - |
| hemophilia A | Recombinant adeno-associated virus serotype 8 (rAAV2/8) vector expressing bioengineered B domain deleted liver-codon-optimized human factor VIII | Orphan Designation | - |