1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| anosmia for isobutyric acid | Multi-vitamin infusion (neonatal formula) | Orphan Designation | - |
| leukoencephalopathy with brain stem and spinal cord involvement-high lactate syndrome | Multi-vitamin infusion (neonatal formula) | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 11 | Multi-vitamin infusion (neonatal formula) | Orphan Designation | - |
| mitochondrial DNA maintenance syndrome | Multi-vitamin infusion (neonatal formula) | Orphan Designation | - |
| spatial visualization, aptitude for | Multi-vitamin infusion (neonatal formula) | Orphan Designation | - |