1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ALG8-congenital disorder of glycosylation | Recombinant human antithrombin III | Orphan Designation | - |
| MPI-congenital disorder of glycosylation | Recombinant human antithrombin III | Orphan Designation | - |
| congenital disorder of glycosylation, type IIw | Recombinant human antithrombin III | Orphan Designation | - |