3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ATTRV30M amyloidosis | a fusion protein of humanized immunoglobulin G1 (IgG1) with a pan amyloid-reactive peptide (p5R) genetically incorporated into the C-terminus of the light chainIodine (I-124) evuzamitide | Orphan Designation | - |
| acquired monoclonal Ig light chain-associated Fanconi syndrome | Iodine (I124) evuzamitide | Orphan Designation | - |
| familial amyloid neuropathy | a fusion protein of humanized immunoglobulin G1 (IgG1) with a pan amyloid-reactive peptide (p5R) genetically incorporated into the C-terminus of the light chainIodine (I-124) evuzamitide | Orphan Designation | - |
| immunoglobulin heavy-and-light chain | Iodine (I124) evuzamitide | Orphan Designation | - |
| primary systemic amyloidosis | Iodine (I124) evuzamitide | Orphan Designation | - |