3
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| anosmia for isobutyric acid | Autologous DNP-conjugated tumor vaccine | Orphan Designation | - |
| double nail for fifth toe | Autologous DNP-conjugated tumor vaccine | Orphan Designation | - |
| hemoglobin--variants for which the chain carrying the mutation 1S unknown or uncertain | Autologous DNP-conjugated tumor vaccine | Orphan Designation | - |
| immunodeficiency 102 | retroviral gamma-c cDNA containing vector | Orphan Designation | - |
| intellectual disability, autosomal dominant 47 | Autologous DNP-conjugated tumor vaccine | Orphan Designation | - |
| modifier, X-linked, for Neurofunctional defects | Autologous DNP-conjugated tumor vaccine | Orphan Designation | - |
| ovarian cancer | DNP-Modified autologous tumor vaccine | Orphan Designation | - |
| severe X-linked mitochondrial encephalomyopathy | retroviral gamma-c cDNA containing vector | Orphan Designation | - |
| spatial visualization, aptitude for | Autologous DNP-conjugated tumor vaccine | Orphan Designation | - |