A healthcare company with 81 FDA-approved drugs and 8 orphan drug designations, it is actively involved in addressing 19 rare diseases, including various forms of chronic lymphocytic leukemia.
8
Orphan Designations
81
FDA Approvals
19
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Rett syndrome | Prismocitrate 18 | Orphan Designation | - |
| acute flaccid myelitis | Anti-CD45 monoclonal antibodiesC1-inhibitor | Orphan Designation | - |
| acute graft versus host disease | Anti-CD45 monoclonal antibodies | Orphan Designation | - |
| acute lymphoblastic leukemia | Anti-CD45 monoclonal antibodies | Orphan Designation | - |
| alcohol abuse | Prismocitrate 18 | Orphan Designation | - |
| cholestasis, progressive familial intrahepatic, 6 | Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio | Orphan Designation | - |
| chronic lymphocytic leukemia/small lymphocytic lymphoma | BENDAMUSTINE HYDROCHLORIDE | - | FDA Approved |
| chronic lymphocytic leukemia/small lymphocytic lymphoma with immunoglobulin heavy chain variable-region gene somatic hypermutation | BENDAMUSTINE HYDROCHLORIDE | - | FDA Approved |
| chronic renal failure syndrome | Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio | Orphan Designation | - |
| congenital total pulmonary venous return anomaly | Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio | Orphan Designation | - |
| diffuse nonepidermolytic palmoplantar keratoderma | Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio | Orphan Designation | - |
| essential thrombocythemia | C1-inhibitor | Orphan Designation | - |
| familial thrombocytosis | C1-inhibitor | Orphan Designation | - |
| hereditary pulmonary alveolar proteinosis | Extraneal (with 7.5% Icodextrin) Peritoneal Dialysis Solutio | Orphan Designation | - |
| neoplastic meningitis | Mafosfamide | Orphan Designation | - |
| nicotine dependence | Prismocitrate 18 | Orphan Designation | - |
| potassium deficiency | POTASSIUM CHLORIDE | - | FDA Approved |
| pregerminal center chronic lymphocytic leukemia/small lymphocytic lymphoma | BENDAMUSTINE HYDROCHLORIDE | - | FDA Approved |
| short bowel syndrome | Arginine butyrate | Orphan Designation | - |