1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Huntington disease | Dihydrotestosterone | Orphan Designation | - |
| fatal familial insomnia | Dihydrotestosterone | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 8a | Dihydrotestosterone | Orphan Designation | - |