2
Orphan Designations
2
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Dravet syndrome | Diacomit | Orphan Designation | - |
| febrile seizures, familial | Diacomit | Orphan Designation | - |
| primary hyperoxaluria | Stiripentol | Orphan Designation | - |