3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| African iron overload | deferoxamine starch conjugate | Orphan Designation | - |
| GRACILE syndrome | deferoxamine starch conjugate | Orphan Designation | - |
| acute flaccid myelitis | deferoxamine starch conjugateDextran and deferoxamine | Orphan Designation | - |
| cholera | deferoxamine starch conjugateDextran and deferoxamine | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | deferoxamine starch conjugateDextran and deferoxamine | Orphan Designation | - |
| neurodegeneration with brain iron accumulation 2A | deferoxamine starch conjugate | Orphan Designation | - |
| sickle cell disease | deferoxamine starch conjugate | Orphan Designation | - |