2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Ebola hemorrhagic fever | aphidicolin | Orphan Designation | - |
| Prader-Willi syndrome | D-tagatose | Orphan Designation | - |
| lethal acantholytic epidermolysis bullosa | aphidicolin | Orphan Designation | - |