2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| encephalopathy due to defective mitochondrial and peroxisomal fission 2 | inBreath airway transplant system | Orphan Designation | - |
| hereditary spastic paraplegia 7 | cellspan esophageal implant | Orphan Designation | - |
| hyper-IgE recurrent infection syndrome 1, autosomal dominant | cellspan esophageal implant | Orphan Designation | - |
| insensitivity to pain with hyperplastic Myelinopathy | inBreath airway transplant system | Orphan Designation | - |
| pancreatic insulin-producing neuroendocrine tumor | cellspan esophageal implant | Orphan Designation | - |
| paraplegia | cellspan esophageal implant | Orphan Designation | - |
| twin to twin transfusion syndrome | inBreath airway transplant system | Orphan Designation | - |