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Bioverativ Therapeutics, Inc. — Rare Disease Pipeline | Kisho | Kisho
Bioverativ Therapeutics, Inc.
Other
3
Orphan Designations
0
FDA Approvals
15
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
RFT1-congenital disorder of glycosylation
ALPROLIX
Orphan Designation
-
Stormorken syndrome
ALPROLIX
Orphan Designation
-
autism
Eloctate
Orphan Designation
-
bleeding disorder, platelet-type, 21
Altuviiio
Eloctate
Orphan Designation
-
bleeding disorder, platelet-type, 22
Altuviiio
Eloctate
ALPROLIX
Orphan Designation
-
bleeding disorder, platelet-type, 25
Altuviiio
Eloctate
Orphan Designation
-
hemophilia A
Altuviiio
Eloctate
Orphan Designation
-
intellectual developmental disorder, X-linked, syndromic, Pilorge type
Eloctate
Orphan Designation
-
intellectual disability-severe speech delay-mild dysmorphism syndrome
Eloctate
ALPROLIX
Orphan Designation
-
lysinuric protein intolerance
ALPROLIX
Orphan Designation
-
moyamoya angiopathy-short stature-facial dysmorphism-hypergonadotropic hypogonadism syndrome
ALPROLIX
Orphan Designation
-
periodic fever-infantile enterocolitis-autoinflammatory syndrome
ALPROLIX
Orphan Designation
-
peripheral primitive neuroectodermal tumor
ALPROLIX
Orphan Designation
-
pheochromocytoma
ALPROLIX
Orphan Designation
-
sitosterolemia 1
ALPROLIX
Orphan Designation
-
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