6
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Hodgkins lymphoma | Talabostat | Orphan Designation | - |
| NF2-related schwannomatosis | bortezomib | Orphan Designation | - |
| acute myeloid leukemia | TalabostatSodium Stibogluconate | Orphan Designation | - |
| chromosome 17q11.2 deletion syndrome, 1.4Mb | bortezomib | Orphan Designation | - |
| malignant pancreatic neoplasm | Talabostat | Orphan Designation | - |
| neurofibromatosis | bortezomib | Orphan Designation | - |
| soft tissue sarcoma | Talabostat | Orphan Designation | - |
| stage II endometrioid carcinoma | Talabostat | Orphan Designation | - |
| stage IVb bladder cancer | Talabostat | Orphan Designation | - |