1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kabuki syndrome 1 | Humanized IgG1kappa monoclonal antibody (anti-HER2 antibody) conjugated to eribulin via a cathepsin-cleavable valine-citrulline linker | Orphan Designation | - |
| Smith-Lemli-Opitz syndrome | Humanized IgG1kappa monoclonal antibody (anti-HER2 antibody) conjugated to eribulin via a cathepsin-cleavable valine-citrulline linker | Orphan Designation | - |
| gastric leiomyosarcoma | Humanized IgG1kappa monoclonal antibody (anti-HER2 antibody) conjugated to eribulin via a cathepsin-cleavable valine-citrulline linker | Orphan Designation | - |
| gastric lymphoma | Humanized IgG1kappa monoclonal antibody (anti-HER2 antibody) conjugated to eribulin via a cathepsin-cleavable valine-citrulline linker | Orphan Designation | - |
| gastric ulcer | Humanized IgG1kappa monoclonal antibody (anti-HER2 antibody) conjugated to eribulin via a cathepsin-cleavable valine-citrulline linker | Orphan Designation | - |
| gastric volvulus, intrathoracic | Humanized IgG1kappa monoclonal antibody (anti-HER2 antibody) conjugated to eribulin via a cathepsin-cleavable valine-citrulline linker | Orphan Designation | - |