1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute intermittent porphyria | Hemin and zinc mesoporphyrin | Orphan Designation | - |
| hepatic porphyria | Hemin and zinc mesoporphyrin | Orphan Designation | - |
| porphyria, acute intermittent, nonerythroid variant | Hemin and zinc mesoporphyrin | Orphan Designation | - |