3
Orphan Designations
4
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Cowden syndrome 1 | SUPREP Bowel Prep Kit | Orphan Designation | - |
| Cowden syndrome 5 | SUPREP Bowel Prep Kit | Orphan Designation | - |
| DYRK1A-related intellectual disability syndrome | sodium sulfate, potassium sulfate, and magnesium sulfate; PEG-3350, sodium chloride, sodium bicarbonate and potassium chloride | Orphan Designation | - |
| anosmia for isobutyric acid | sodium sulfate, potassium sulfate, and magnesium sulfate; PEG-3350, sodium chloride, sodium bicarbonate and potassium chlorideSUPREP Bowel Prep Kit | Orphan Designation | - |
| functional colonic disease | sodium sulfate, magnesium sulfate, potassium chloride | Orphan Designation | - |
| hemoglobin--variants for which the chain carrying the mutation 1S unknown or uncertain | SUPREP Bowel Prep Kit | Orphan Designation | - |
| neuroacanthocytosis | sodium sulfate, potassium sulfate, and magnesium sulfate; PEG-3350, sodium chloride, sodium bicarbonate and potassium chloride | Orphan Designation | - |
| polycystic kidney disease 1 | SUPREP Bowel Prep Kit | Orphan Designation | - |
| punctate palmoplantar keratoderma type III | SUPREP Bowel Prep Kit | Orphan Designation | - |