1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| plasma cell myeloma | B-cell maturation antigen (BCMA)-chimeric antigen receptor (CAR)-induced pluripotent stem cell (iPSC)-derived invariant natural killer T (iNKT) cells [BCMA-CAR-ipsNKT cells] | Orphan Designation | - |