1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | BCL-005 (fused (hybrid) melanoma-dendritic cells) | Orphan Designation | - |
| Finnish type amyloidosis | BCL-005 (fused (hybrid) melanoma-dendritic cells) | Orphan Designation | - |
| lysinuric protein intolerance | BCL-005 (fused (hybrid) melanoma-dendritic cells) | Orphan Designation | - |