4
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Roberts-SC phocomelia syndrome | 2-(3-diethylaminopropyl)-8,8-dipropyl-2-azaspiro [4,5] decan dimaleate | Orphan Designation | - |
| acute lymphoblastic leukemia | Liposomal annamycin | Orphan Designation | - |
| acute myeloid leukemia | Liposomal annamycin | Orphan Designation | - |
| carcinoid syndrome | 2-(3-Diethylaminopropyl)-8,8-dipropyl-2-azaspiro[4,5] decane dimaleate | Orphan Designation | - |
| digestive system neuroendocrine neoplasm | 2-(3-Diethylaminopropyl)-8,8-dipropyl-2-azaspiro[4,5] decane dimaleate | Orphan Designation | - |
| ectopic Cushing syndrome | 2-(3-Diethylaminopropyl)-8,8-dipropyl-2-azaspiro[4,5] decane dimaleate | Orphan Designation | - |
| indolent plasma cell myeloma | 2-(3-diethylaminopropyl)-8,8-dipropyl-2-azaspiro [4,5] decan dimaleate | Orphan Designation | - |
| non-secretory plasma cell myeloma | 2-(3-diethylaminopropyl)-8,8-dipropyl-2-azaspiro [4,5] decan dimaleate | Orphan Designation | - |
| osteosclerotic plasma cell myeloma | 2-(3-diethylaminopropyl)-8,8-dipropyl-2-azaspiro [4,5] decan dimaleate | Orphan Designation | - |
| plasma cell myeloma | 2-(3-diethylaminopropyl)-8,8-dipropyl-2-azaspiro [4,5] decan dimaleate | Orphan Designation | - |
| smoldering plasma cell myeloma | 2-(3-diethylaminopropyl)-8,8-dipropyl-2-azaspiro [4,5] decan dimaleate | Orphan Designation | - |