2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| infratentorial cancer | Adenoviral vector expressing Herpes simplex virus thymidine kinase gene | Orphan Designation | - |
| malignant pancreatic neoplasm | aglatimagene besadenovec | Orphan Designation | - |
| mismatch repair cancer syndrome 1 | Adenoviral vector expressing Herpes simplex virus thymidine kinase gene | Orphan Designation | - |
| rhabdoid tumor predisposition syndrome 1 | Adenoviral vector expressing Herpes simplex virus thymidine kinase gene | Orphan Designation | - |