2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| post 5-alpha-reductase inhibitors treatment syndrome | selective nonsteroidal FXR agonist | Orphan Designation | - |
| post-treatment Lyme disease syndrome | selective nonsteroidal FXR agonist | Orphan Designation | - |
| primary sclerosing cholangitis | 3-(4-((3-endo)-3-((5-cyclopropyl-3-(2,6-dichlorophenyl)isoxazol-4- yl)methoxy)-8-azabicyclo[3.2.1]octan-8-yl)-2-fluorophenyl)-1,2,4-oxadiazol-5(4H)-one | Orphan Designation | - |
| treatment-refractory schizophrenia | selective nonsteroidal FXR agonist | Orphan Designation | - |