1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Down syndrome | Aloprim for Injection | Orphan Designation | - |
| NTRK fusion positive cancer | Aloprim for Injection | Orphan Designation | - |
| Noonan syndrome 1 | Aloprim for Injection | Orphan Designation | - |
| RET fusion positive cancer | Aloprim for Injection | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Aloprim for Injection | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | Aloprim for Injection | Orphan Designation | - |