7
Orphan Designations
0
FDA Approvals
13
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Ewing sarcoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| Ewing sarcoma of bone | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| Waldenstrom macroglobulinemia | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| alveolar soft part sarcoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| extraskeletal Ewing sarcoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| glioma | 18-(p-[124I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| lymphoplasmacytic lymphoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| lymphoplasmacytic lymphoma without IgM production | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| neuroblastoma | 18-(p-[131]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| osteosarcoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| plasma cell myeloma | 1 8-(p[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| soft tissue sarcoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |
| undifferentiated pleomorphic sarcoma | 18-(p-[131I]-iodophenyl)octadecyl phosphocholine | Orphan Designation | - |