1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Renpenning syndrome | Lantidra | Orphan Designation | - |
| brittle cornea syndrome | Lantidra | Orphan Designation | - |
| leukoencephalopathy, diffuse hereditary, with spheroids 1 | Lantidra | Orphan Designation | - |
| orofaciodigital syndrome I | Lantidra | Orphan Designation | - |
| polycystic kidney disease 1 | Lantidra | Orphan Designation | - |
| trichohepatoenteric syndrome | Lantidra | Orphan Designation | - |