1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| NF2-related schwannomatosis | Transforming growth factor-beta 2 | Orphan Designation | - |
| fountain syndrome | Transforming growth factor-beta 2 | Orphan Designation | - |
| idiopathic non-lupus full-house nephropathy | Transforming growth factor-beta 2 | Orphan Designation | - |