15
Orphan Designations
0
FDA Approvals
31
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Behcet disease | Remicade | Orphan Designation | - |
| Crohn disease | Remicade | Orphan Designation | - |
| MALT lymphoma | Human Anti-tumor Necrosis factor alpha monoclonal antibody | Orphan Designation | - |
| TORCH syndrome | Human IgM monoclonal antibody (C-58) To CMV | Orphan Designation | - |
| anosmia for isobutyric acid | Remicade | Orphan Designation | - |
| autoinflammatory syndrome, familial, Behcet-like 1 | Remicade | Orphan Designation | - |
| birdshot chorioretinopathy | Human Anti-tumor Necrosis factor alpha monoclonal antibody | Orphan Designation | - |
| chronic inflammatory demyelinating polyradiculoneuropathy | golimumabInfliximab | Orphan Designation | - |
| chronic primary adrenal insufficiency | golimumabInfliximab | Orphan Designation | - |
| chronic recurrent multifocal osteomyelitis | golimumabInfliximab | Orphan Designation | - |
| congenital microcephaly - severe encephalopathy - progressive cerebral atrophy syndrome | Remicade | Orphan Designation | - |
| cytomegalovirus infection | Human IgM monoclonal antibody (C-58) To CMV | Orphan Designation | - |
| developmental and epileptic encephalopathy 6B | Remicade | Orphan Designation | - |
| developmental and epileptic encephalopathy, 41 | Remicade | Orphan Designation | - |
| glycogen storage disease VI | Remicade | Orphan Designation | - |
| heterotopia, periventricular, X-linked dominant | Nebacumab | Orphan Designation | - |
| inflammatory bowel disease 1 | Remicade | Orphan Designation | - |
| interstitial lung disease specific to childhood | Remicade | Orphan Designation | - |
| juvenile idiopathic arthritis | infliximab | Orphan Designation | - |
| malignant pancreatic neoplasm | carlumabMonoclonal antibody 17-1a | Orphan Designation | - |
| multiple sclerosis | Chimeric M-T412 (human-murine) IgG monoclonal anti-CD4 | Orphan Designation | - |
| myocarditis | Indium In 111 murine monoclonal antibody FAB to myosin | Orphan Designation | - |
| neonatal encephalomyopathy-cardiomyopathy-respiratory distress syndrome | Remicade | Orphan Designation | - |
| neurodevelopmental disorder with seizures, microcephaly, and brain abnormalities | Nebacumab | Orphan Designation | - |
| osteoporosis-pseudoglioma syndrome | Remicade | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Remicade | Orphan Designation | - |
| pediatric-onset Graves disease | Remicade | Orphan Designation | - |
| phacoanaphylactic uveitis | Human Anti-tumor Necrosis factor alpha monoclonal antibody | Orphan Designation | - |
| severe intellectual disability-short stature-behavioral abnormalities-facial dysmorphism syndrome | Remicade | Orphan Designation | - |
| temporal arteritis | infliximab | Orphan Designation | - |
| thrombocytopenia 11 with multiple congenital anomalies and dysmorphic facies | Nebacumab | Orphan Designation | - |