1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Becker muscular dystrophy | L-aminocarnityl-succinyl-leucyl-argininal-diethylacetal | Orphan Designation | - |
| Duchenne muscular dystrophy | L-aminocarnityl-succinyl-leucyl-argininal-diethylacetal | Orphan Designation | - |
| Erb palsy | L-aminocarnityl-succinyl-leucyl-argininal-diethylacetal | Orphan Designation | - |